Opal Sandy, aged 18 months, was born completely deaf due to condition auditory neuropathy

  • witty_username@feddit.nl
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    6 months ago

    No
    The gene therapy is applied locally. They operate on the ear to enable access to the relevant tissue and then apply the therapy. So it should only affect cells in the ear.
    Additionally, it is unclear to me whether the therapeutic gene is integrated into the genome. It might not be.
    For transmission to offspring, you would need to edit germ line cells (sex cells) and you would need to integrate the gene into the genome.